▍Medication for Rare Diseases
Medication for Rare Diseases
Medication for Rare Diseases
|
Disease |
Medication |
|---|---|
|
urea cycle disorder |
Arginine HCL Injection |
|
Homocystinuria |
Cystadane |
|
Congenital hyperammonemia caused by abnormal urea metabolism due to citrulline deficiency |
Stimol |
|
Acute and chronic treatment of secondary carnitine deficiency patients with congenital genetic abnormalities of metabolism |
L-Carnitine |
|
urea cycle disorder |
Buphenyl |
|
Tetrahydrobiopterin dificiency |
BH4 |
|
The hyperinsulinism/hyperammonemia syndrome |
Proglycem (Diazoside) |
|
Non-Ketotic hyperglycinemia |
Sodium Benzoate |
|
Porphyria |
Normosang |
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